Marilyn J. Field and Thomas F. Boat, Editors; Committee on Accelerating Rare Diseases Research and Orphan Product Development; Institute of Medicine
Rare diseases collectively affect millions of Americans of all ages, but developing drugs and medical devices to prevent, diagnose, and treat these conditions is challenging. The Institute of Medicine (IOM) recommends implementing an integrated national strategy to promote rare diseases research and product development.
Marilyn J. Field and Thomas F. Boat, Editors; Committee on Pediatric Studies Conducted Under the Best Pharmaceuticals for Children Act (BPCA) and the Pediatric Research Equity Act (PREA); Institute of Medicine